Protocol for initiation of miglustat treatment in NP-C. Reproduced

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Last updated 21 setembro 2024
Protocol for initiation of miglustat treatment in NP-C. Reproduced
Protocol for initiation of miglustat treatment in NP-C. Reproduced
Protocol for initiation of miglustat treatment in NP-C. Reproduced with
Protocol for initiation of miglustat treatment in NP-C. Reproduced
Substrate reduction therapy in the infantile form of Tay-Sachs disease
Protocol for initiation of miglustat treatment in NP-C. Reproduced
Protocol for initiation of miglustat treatment in NP-C. Reproduced with
Protocol for initiation of miglustat treatment in NP-C. Reproduced
Protocol for initiation of miglustat treatment in NP-C. Reproduced with
Protocol for initiation of miglustat treatment in NP-C. Reproduced
Distinct Niemann-Pick Disease Type C Clinical, Cytological, and Biochemical Phenotype in an Adult Patient With 1 Mutated, Overexpressed NPC1 Allele - Julia Jecel, Klaus Harzer, Eduard Paschke, Stefanie Beck-Wödl, Peter Bauer, Milos
Protocol for initiation of miglustat treatment in NP-C. Reproduced
IJMS, Free Full-Text
Protocol for initiation of miglustat treatment in NP-C. Reproduced
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Protocol for initiation of miglustat treatment in NP-C. Reproduced
Frontiers Adult-Onset Niemann–Pick Disease Type C: Rapid Treatment Initiation Advised but Early Diagnosis Remains Difficult
Protocol for initiation of miglustat treatment in NP-C. Reproduced
Correlation of age of onset and clinical severity in Niemann–Pick disease type C1 with lysosomal abnormalities and gene expression
Protocol for initiation of miglustat treatment in NP-C. Reproduced
Pronounced Therapeutic Benefit of a Single Bidirectional AAV Vector Administered Systemically in Sandhoff Mice: Molecular Therapy
Protocol for initiation of miglustat treatment in NP-C. Reproduced
Tolerance of chronic HDACi treatment for neurological, visceral and lung Niemann-Pick Type C disease in mice
Protocol for initiation of miglustat treatment in NP-C. Reproduced
Pluronic based β-cyclodextrin polyrotaxanes for treatment of Niemann-Pick Type C disease
Protocol for initiation of miglustat treatment in NP-C. Reproduced
Chronic Cyclodextrin Treatment of Murine Niemann-Pick C Disease Ameliorates Neuronal Cholesterol and Glycosphingolipid Storage and Disease Progression

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