Generation of HEXA-deficient hiPSCs from fibroblasts of a Tay

Human iPSC line TSD-01-hiPSC was generated from fibroblasts of a patient with infantile Tay-Sachs disease (TSD). The patient is compound heterozygous …

Myelination and Node of Ranvier Formation in a Human Motoneuron–Schwann Cell Serum-Free Coculture

Engineering of Human-Induced Pluripotent Stem Cells for Precise Disease Modeling

Frontiers The Linkage Phase of the Polymorphism KCNH2-K897T Influences the Electrophysiological Phenotype in hiPSC Models of LQT2

Role of induced pluripotent stem cells in lysosomal storage diseases - ScienceDirect

Chemical mutagenesis of a GPCR ligand: Detoxifying “inflammo-attraction” to direct therapeutic stem cell migration

Human Induced Pluripotent Stem Cells as a Platform for Personalized and Precision Cardiovascular Medicine

Delineating the Neuropathology of Lysosomal Storage Diseases Using Patient-Derived Induced Pluripotent Stem Cells

Frontiers Emerging Concepts in Vector Development for Glial Gene Therapy: Implications for Leukodystrophies

Creation of isogenic control (HEXB-corrected) iPS cells and generation